Our focus is to develop life-transforming therapies for people living with serious neuromuscular diseases. We are utilizing our FORCE™ platform to deliver therapies to muscle and the central nervous system (CNS) with the goal of stopping or reversing disease progression. We have assembled an exceptional team with deep experience in neuromuscular disease, rare disorders, drug development, and manufacturing and commercialization of novel therapeutics. We have also established a scientific advisory board comprised of leading experts in the neuromuscular disease drug discovery and development, who share our mission.

Because together, we are stronger.